About
12
Publications
318
Reads
How we measure 'reads'
A 'read' is counted each time someone views a publication summary (such as the title, abstract, and list of authors), clicks on a figure, or views or downloads the full-text. Learn more
19
Citations
Citations since 2017
Publications
Publications (12)
This white paper discusses the benefits and uses of real-world evidence as well as the power of digital technology in RWE generation.
OBJECTIVES
To identify common methods for the estimation of healthcare resource use (HRU) and to assess their strengths and weaknesses.
METHODS
A targeted search of the MEDLINE database, databases for economic evaluations, and HTA websites was conducted to identify articles reporting on HRU data-collection methods. The search was indication- and t...
Introduction
Myasthenia gravis (MG) is a rare, chronic, autoimmune disease, mediated by immunoglobulin G antibodies, which causes debilitating muscle weakness. As with most rare diseases, there is little patient-reported data with which to understand and address patient needs. This study explores the impact of MG in the real world from the patient...
Background and Objective
Transfusion-dependent β-thalassemia (TDT) is a rare genetic disease characterized by a deficiency of functional β-globin, ultimately leading to lifelong dependence on blood transfusions. There is little patient- and caregiver-reported data with which to understand the holistic and societal impact of TDT. The objective of th...