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  • Jul 2012
    Prix Henri Chaigneau
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My current goal is to establish gene therapy as the treatment of choice for all types of severe haemophilia. Since we demonstrated safety and efficacy of gene transfer for haemophilia B we have evidently convinced all the major pharmaceutical companies involved in synthetic factor production that this is feasible as they have now invested heavily in gene therapy. Meanwhile we continue to pioneer novel vectors with Haemophilia A and factor VII deficiency as our next targets.

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